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Company

Ionis Pharmaceuticals

Pharmaceutical intelligence for Ionis Pharmaceuticals with 4 indexed intelligence signals across regulatory, clinical, competitive, and market developments.

Signals
2
Catalysts
2
Assets
3

Recent signals(2)

ClinicalJuly 13, 2026

Ionis Pharmaceuticals Evaluates Sapablursen in Polycythemia Vera Patients

Ionis Pharmaceuticals is conducting a study to assess the efficacy of sapablursen in reducing phlebotomy frequency and improving quality of life in polycythemia vera patients.

RegulatoryJune 27, 2026

FDA Grants Priority Review for TRYNGOLZA Autoinjector Submission

The FDA has granted priority review for the supplemental application of TRYNGOLZA (olezarsen sodium) autoinjector by Ionis Pharmaceuticals.

Upcoming catalysts(1)

FDA Approval

Ionis Pharmaceuticals — Donidalorsen

Approval would validate Ionis RNA platform in prophylactic rare disease setting.

August 20, 2026 · NDA/BLA

Regulatory activity

(1)
RegulatoryJune 27, 2026

FDA Grants Priority Review for TRYNGOLZA Autoinjector Submission

The FDA has granted priority review for the supplemental application of TRYNGOLZA (olezarsen sodium) autoinjector by Ionis Pharmaceuticals.

Clinical activity(1)

ClinicalJuly 13, 2026

Ionis Pharmaceuticals Evaluates Sapablursen in Polycythemia Vera Patients

Ionis Pharmaceuticals is conducting a study to assess the efficacy of sapablursen in reducing phlebotomy frequency and improving quality of life in polycythemia vera patients.

Competitive activity

No signals indexed for this entity yet.

Assets

Donidalorsen →
Ionis →
TRYNGOLZA →

Therapeutic areas

Hematology →
Neurology →
Neurology · RNA-targeted therapy →
Rare Disease →
RNA-targeted therapy →

Indications

Hereditary angioedema →

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